Vertex Pharmaceuticals and CRISPR Therapeutics Announce Authorization of the First CRISPR/Cas9 Gene-Edited Therapy, CASGEVY

Vertex Pharmaceuticals and CRISPR Therapeutics Announce Authorization of CASGEVY

Conditional Approval for Both Sickle Cell Disease and Transfusion Dependent Beta Thalassemia

Vertex Pharmaceuticals (VRTX) and CRISPR Therapeutics (CRSP) today announced that the United Kingdom (U.K.) Medicines and Healthcare products Regulatory Agency (MHRA) granted them conditional marketing authorization for CASGEVYTM (exagamglogene autotemcel [exa-cel]), a CRISPR/Cas9 gene . . .

This content is for paid subscribers.
Please click here to subscribe or here to log in.