Mirum Pharmaceuticals
Mirum Pharmaceuticals (MIRM) is a leading rare disease company with a global footprint of approved products and a broad pipeline of investigational medicines. Purpose-built to bring forward breakthrough medicines for people with overlooked conditions, Mirum combines deep rare disease expertise with strong connections to patient communities.
From the Experts
Tatyana Kushner, M.D., MSCE, Associate Professor of . . .
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Impacting News
March 6, 2026
