Author: Prohost

PTC Therapeutics Provides Corporate Update and Reports First Quarter 2025 Financial Results

PTC Therapeutics On May 6, 2025, PTC Therapeutics (PTCT) announced a corporate update and financial results for the first quarter ended March 31, 2025. We loved the firm’s strong revenue performance of $190 million,  the positive CHMP opinion for Sephience™ (sepiapterin) received in April 2025, and, important is the  NDA review remained on track for July 29, 2025, PDUFA date, the . . . This …

Alnylam Pharmaceuticals Reported Its Q1 2025 Financial Results and Highlights Recent Period Progress

Alnylam Pharmaceuticals Synopsis  Today, May 1, 2025 - Alnylam Pharmaceuticals (ALNY), the leading RNAi therapeutics company reported its consolidated financial results for the first quarter ended March 31, 2025 and reviewed recent business highlights. From Alnylam Pharmaceuticals Yvonne Greenstreet, M.D., Chief Executive Officer of Alnylam Pharmaceuticals, said, “2025 is off to a remarkable start, having ended the first quarter with U.S . . . This …

Important Biotechnology Companies’ News, Plus News from the American Association for Cancer Research and More 

Important News from AbbVie AbbVie (ABBV) submitted a biological license application (BLA) to the United States’ FDA for its sensational product trenibotulinumtoxinE (TrenibotE), which reduces frown lines between the eyebrows, known as glabellar lines. The Product TrenibotE is a botulinum toxin of serotype E with short effects of a long duration for the users. The product is safer than the existing . . . This …

Vera Therapeutics ORIGIN Phase 3 Trial for Atacicept in IgAN

We still believe in many outperforming biotechnology firms whose stocks are underestimated on Wall Street. We believe these firms are outperforming in science but not yet in the Stock Market. We will continue to post them on our website. One of the firms that we recently liked after assessment is Vera Therapeutics.   Vera Therapeutics Vera Therapeutics (

Why and How the Stock Market Rallied Plus a Combination That Treated a Severe Colorectal Cancer

Today's Stock Market Rally Today, Wednesday, April 9, 2025 the news started with Trump announcing a '90-day pause' on tariffs for most countries. What happened next was a rallying Stock Market with the Dow, the S&P 500 and the Nasdaq soaring.   The S&P 500 climbed up around 8%, the Nasdaq Composite rallied 10% and the Dow Jones Industrial Average was up over 7%. President …

Why Rhythm Pharmaceuticals Stock Rallied While The Market Was Tumbling

Rhythm Pharmaceuticals Rally Last week, almost all the stocks tumbled. On Monday, the first day of the current week, we could see biotech firms usually moving up after good news, which didn’t occur during the few bad days of the market's tumbling.  One of the health firm’s sectors Rhythm Pharmaceuticals (RYTM) rallied after having more promising news . . . This content is for paid subscribers. …

Novo Nordisk at ACC 2025: Ozempic® with Once Weekly Semaglutide 1mg Shown to Improve Walking Distance and Quality of Life in Adults with Type 2 Diabetes and Peripheral Artery Disease

Novo Nordisk in the NEWS Novo Nordisk (NVO) presented the full results from STRIDE, a phase 3b peripheral artery disease (PAD) outcomes trial investigating the effects of once-weekly injectable Ozempic® (semaglutide 1.0 mg) in adults with type 2 diabetes and PAD, at the American College of Cardiology's (ACC) Annual Scientific Session and Expo in Chicago, US . . . This content is for paid subscribers. …

The U.S. FDA Approved Alnylam Pharmaceuticals’ Product Qfitlia to Treat Hemophilia A or B With or Without Inhibitors

Stock Market Plummet and Alnylam Pharmaceuticals Good News Today, the stock market is plummeting. In fact, most stocks have been falling since early morning. The reason has nothing to do with the company’s activities. The best companies with the best science and scientists are sinking into the bottom of the deepest ocean today. Even though the Stock Market is surrounded by negativity, we will still …

Wave Life Sciences Announced What Could be Excellent News in Treating Duchenne Muscular Dystrophy

Wave Life Sciences On March 26, 2025, Wave Life Sciences (WVE) announced positive data from the Phase 2 FORWARD-53 trial of WVE-N531, an exon skipping oligonucleotide being investigated in boys with Duchenne muscular dystrophy (DMD) who are amenable to exon 53 skipping. FORWARD-53 Trial demonstrates sustained and industry-leading exon . . . This content is for paid subscribers. Please click here to subscribe or here to log …

BridgeBio Pharma to Present Cardiovascular Outcomes Data in Patients with Variant and Wild-Type Transthyretin Amyloid Cardiomyopathy at the ACC Annual Scientific Sessions

BridgeBio Pharma Today, March 24, 2025, BridgeBio Pharma, Inc. (BBIO) announced that cardiovascular outcomes data in patients with variant and wild-type ATTR-CM from the ATTRibute-CM, its Phase 3 study of acoramidis in ATTR-CM, will be shared in a flatboard poster presentation at the American College . . . This content is for paid subscribers. Please click here to subscribe or here to log in.

Results from PTC Therapeutics’ Latest Presentation

PTC Therapeutics Inc On March 20, 2025, PTC Therapeutics, Inc. (PTCT) shared new data from the Phase 3 APHENITY trial and subsequent open-label extension study at the 2025 American College of Medical Genetics and Genomics (ACMG) Annual Clinical Genetics Meeting. These data provide further evidence of the potential meaningful benefits of sepiapterin treatment for the full spectrum of phenylketonuria (PKU . . . This content is for paid …

FDA Approved Alnylam Pharmaceuticals sNDA for AMVUTTRA® – A Treatment for Cardiomyopathy of Wild-Type or Hereditary Transthyretin-Mediated Amyloidosis in Adults to Reduce Cardiovascular Mortality, Cardiovascular Hospitalizations and Urgent Heart Failure Visits

Alnylam Pharmaceuticals in the NEWS March 20, 2025, Alnylam Pharmaceuticals (ALNY) - the leading RNAi therapeutics company, today announced that the U.S. FDA has approved the supplemental New Drug Application (sNDA) for its RNAi therapeutic, AMVUTTRA® (vutrisiran), for the treatment of the cardiomyopathy of wild-type or hereditary transthyretin-mediated amyloidosis (ATTR-CM) in adults to . . . This content is for paid subscribers. Please click here to subscribe or …

Two Companies: Pyxis Oncology Financial Results and Sarepta Therapeutics Unwarranted Selloff

Pyxis Oncology in the NEWS Pyxis Oncology Reports Fourth Quarter and Full Year 2024 Financial Results and Provides Business Update On March 18, 2025, Pyxis Oncology (PYXS) - a clinical-stage firm developing next-generation therapeutics for difficult-to-treat cancers, reported financial results for the year and quarter ending December 31, 2024, and provided a business update. From Pyxis Oncology Lara . . . This content is for paid …

Altimmune, AstraZeneca and Alnylam Pharmaceuticals

Altimmune  Altimmune (ALT) stock soared last Friday after speculation of a takeover by three large companies.  The speculation died today. Nevertheless, other news about this firm could be important, especially from  Altimmune itself. The firm announced that it will assess the potential of GLP . . . This content is for paid subscribers. Please click here to subscribe or here to log in.

A Little About the Stock Market and Some News from Johnson & Johnson

With a bad market and a lot of talk about recession and shutting down the Government, with most stocks tanking, in the middle of this chaos some biotech companies, that we selected for investment, have beaten the bad news and moved up, instead of sinking to the bottom of an uneasy ocean. These stocks closed today at: Stock Symbol Price Change

AstraZeneca: Imfinzi-based Regimen Demonstrated Statistically Significant and Clinically Meaningful Improvement in Event-free Survival in Resectable Early-Stage Gastric and Gastroesophageal Junction Cancers

AstraZeneca AstraZeneca (AZN) has positive high-level results from the MATTERHORN Phase III trial, which showed perioperative treatment with AstraZeneca’s Imfinzi (durvalumab) in combination with standard-of-care FLOT (fluorouracil, leucovorin, oxaliplatin, and docetaxel) chemotherapy demonstrated a statistically significant and clinically meaningful improvement in the primary endpoint of event-free survival (

ARS Pharmaceuticals Announces FDA Approval of neffy® for Type I Allergic Reactions, Including Anaphylaxi in Pediatric Patients   

ARS Pharmaceuticals SAN DIEGO, March 05, 2025 (GLOBE NEWSWIRE), ARS Pharmaceuticals (SPRY) announced that the U.S. FDA has approved neffy® 1 mg (epinephrine nasal spray) for the treatment of Type I Allergy reactions, including anaphylaxis, in children who are aged 4 years and older and weigh 15 to < 30 kilograms (33 to < 66 lb.). This approval represents the first significant innovation in epinephrine delivery for …

Moderna Receives Medicines and Healthcare Products Regulatory Agency Marketing Authorization in the UK for RSV Vaccine

Moderna On February 28, 2025, Moderna (MRNA) announced that the Medicines and Healthcare products Regulatory Agency (MHRA) in the UK has granted marketing authorization for mRESVIA (mRNA-1345), indicated for active immunization for the prevention of lower respiratory tract disease (LRTD) caused by . . . This content is for paid subscribers. Please click here to subscribe or here to log in.