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HomeArticlesToday's HighlightsRegenxbio: Promising Results from RGX-121 Gene Therapy for Mucopolysaccharidosis Type II (MPS II)
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Regenxbio: Promising Results from RGX-121 Gene Therapy for Mucopolysaccharidosis Type II (MPS II)

Regenxbio Results from RGX-121 for MPSII Regenxbio ( RGNX ) announced interim data from Phase I/II trial of RGX-121 for Mucopolysaccharidosis Type II ( MPS II) . RGX-121  is designed to deliver the ge...
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