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PTC Therapeutics: Results of DMD Trial Are Good for Approval

PTC Therapeutics’ (PTCT) Duchenne muscular dystrophy drug (DMD) Translama failed to demonstrate a statistically significant improvement in distance traveled over the six-minute walk test, but it has n...
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BioMarin Pharmaceutical (BMRN)
PTC Therapeutics (PTCT)
Sarepta Therapeutics (SRPT)

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